A potentially viable treatment for not one, not two, but Three Acute Porphyrias is getting closer by the day. The chance of an available RNAi treatment very soon is great, and YOU could be part of what could be Porphyria History.
Alnylam has registered a clinical trial, NCT02240784 at the website www.clinicaltrials.gov, which is recruiting participants right now at three US facilities. The website below will give you all of the information on contacting Alnylam for participating in their current EXPLORE trial and study.
Porphyrians who want to participate in this study need to be diagnosed with one of three acute hepatic porphyrias: AIP, HCP, and/or VP. It does not stipulate on the website that the diagnosis be through biochemical, genetic, or other diagnostic means, but be prepared to back up any diagnosis with documentation if you have it.
According to site, there are no intermediaries for applying for this study. Go directly to Alnylam at the contact numbers provided on the link below, and they will provide you with all of the necessary contact information for the three currently participating facilities. There is no indication that this study is in any way connected to any existing studies being conducted by any other organization.
Go! Make history! Be a part of what could be a truly life saving treatment for three horrible disorders.
http://www.clinicaltrials.gov/ct2/show/NCT02240784?term=ALN-AS1&rank=1
Porphyria's Hater 